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Research unit
INNOSUISSE
Project number
114.430 IP-LS
Project title
PROtein S targeting to prevent BLEEDing

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Abstract
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CategoryText
Key words
(English)
Life sciences, Pharmaceuticals
Abstract
(English)
Hemophilia, impacting over 1.125 million people globally, is addressed by SLN140, a small interfering RNA therapy targeting protein S to prevent bleeding. Preclinical studies on its concept and safety aim for regulatory approval for a first-in-man study.