Small molecule drug for the treatment of myotonic dystrophy

Research unit

INNOSUISSE

Project number

102.272 IP-LS

Project title

Small molecule drug for the treatment of myotonic dystrophy

Texts for this project

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Key words	-	-	-
Abstract	-	-	-

Category	Text
Key words (English)	Life sciences, Human medicine
Abstract (English)	The aim of the project is to obtain pre-clinical development of two patent-protected small molecule drug candidates in animal models for the treatment of myotonic dystrophy. The outcome will generate IND-enabling data for further validation in non-human primates and eventual clinical phase entry.