A novel treatment of GM1-gangliosidosis

Research unit

INNOSUISSE

Project number

62242.1 IP-LS

Project title

A novel treatment of GM1-gangliosidosis (Innolink: 102.301 IP-LS)

Texts for this project

	German	French	Italian	English
Short description		-	-
Abstract		-	-	-

Category	Text
Short description (German)	A novel treatment of GM1-gangliosidosis (Innolink: 102.301 IP-LS)
Short description (English)	A novel treatment of GM1-gangliosidosis
Abstract (German)	Dorphan has shown that Aloxistatin has a therapeutic activity in cells from GM1-gangliosidosis patients. Aloxistatin is a poor drug and has a low brain penetration. We have discovered molecules derived from it and we want to select the best out of them to offer a valuable therapy to the patients.