New Precision Gene Therapies for Amyotrophic Lateral Sclerosis

• Unité de recherche: INNOSUISSE
• Numéro de projet: 52250.1 IP-LS
• Titre du projet anglais: New Precision Gene Therapies for Amyotrophic Lateral Sclerosis

Description succincte (Allemand)

New Precision Gene Therapies for Amyotrophic Lateral Sclerosis

Description succincte (Anglais)

New Precision Gene Therapies for Amyotrophic Lateral Sclerosis

Résumé des résultats (Abstract) (Allemand)

Amyotrophic lateral sclerosis (ALS) is a deadly neurodegenerative disease. We have developed a precision gene therapy platform to treat ALS. The goal of this project is to characterize and validate 2 new targets in ALS which have the potential for a gene therapy treatment of various subtypes of ALS.