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Research unit
INNOSUISSE
Project number
34870.1 IP-LS
Project title
Gene therapy for LAMA2 MD / MDC1A

Texts for this project
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Short description
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Abstract
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CategoryText
Short description
(German)
Gene therapy for LAMA2 MD / MDC1A
Short description
(English)
Gene therapy for LAMA2 MD / MDC1A
Abstract
(German)
Muscular dystrophies are untreatable, fatal diseases. Previous mouse experiments showed that two linker proteins prevent early lethality and stabilize muscle function. We now aim to deliver the linker proteins by AAV9 vectors to test whether this method can be used to treat human patients.