Titre du projet
Proof of Concept Study - Understanding Mechanisms of Action of Newly Developed Non-Competitive Pharmacological Chaperones on Protein Quality Control in Rare Pediatric Lysosomal Storage Diseases
Titre du projet anglais
Proof of Concept Study - Understanding Mechanisms of Action of Newly Developed Non-Competitive Pharmacological Chaperones on Protein Quality Control in Rare Pediatric Lysosomal Storage Diseases